文献类型：期刊文献

英文题名：Safety and Efficacy of Dalnacogene Ponparvovec (BBM-H901) in Moderate to Severe Adult Hemophilia B Participants: Long Term Follow-Up Data in an Early Phase Pilot Study

作者：Xue, Feng[1,2];Zhang, Lei[1,2];Xiao, Xiao[3];Wu, Xia[4];Sun, Yujie[5]

机构：[1]Chinese Acad Med Sci, Inst Hematol & Blood Dis Hosp, Natl Clin Res Ctr Hematol Dis, Tianjin, Peoples R China;[2]Ctr Diag & Treatment Thrombosis & Hemostasis, Tianjin, Peoples R China;[3]Belief Med Technol Shanghai Co Ltd, Shanghai, Peoples R China;[4]East China Univ Sci & Technol, Sch Pharm, Shanghai, Peoples R China;[5]Takeda China Int Trading Co, Beijing, Peoples R China

年份：2026

卷号：32

起止页码：60

外文期刊名：HAEMOPHILIA

收录：;WOS:【SCI-EXPANDED(收录号:WOS:001781126100090)】；

语种：英文

外文关键词：BBM-H901; gene therapy; Hemophilia B